A single dose of Crispr-Cas9 therapy has been shown to have very useful effect on patients with hereditary angioedema. The DNA cutting and pasting system has proven to have very potent use in addressing the genetic condition. Angioedema patients that received a single dose of the gene therapy Crispr-Cas9 had little or no symptoms ofContinue reading “Crispr-Cas9 gene therapy remedies harsh symptoms of hereditary angioedema”
Tag Archives: Genetics
11 year old boy hears for the first time after novel gene therapy
An 11 year old boy who could only use self-invented sign language to communicate from birth, had his hearing restored after receiving the Eli Lilly’s sponsored otoferlin gene therapy.